Research highlight
Hope for a Rare Genetic Disease
GNAO1-related neurodevelopmental disorders were discovered only in the past decade, and are thought to affect at least hundreds of children around the world.

Rhes Protein Key in Spread of Huntington’s…
Nanotube tunnels that act like roadways capable of transporting cargo between cells can transmit a toxic protein linked to Huntington’s disease, a…

Search for Safer Pain Relief Advances with New…
“The compound SR-17018 is the first biased agonist of the mu opioid receptor that does not lead to tolerance with chronic use,” says Stahl, a…

Potential Treatment for ALS, Frontotemporal…
Disney designed the ALS compound by applying nearly 15 years of research finding druggable structures on RNA.
